| Endocrinology |
Tollefsen |
Genentech, Inc. |
PMS II Study |
| Dermatology |
Siegfried |
Amgen |
Evaluate Safety of Etanercept in Pediatric Patients with Plaque Psoriasis |
| Pulmonary |
Noyes |
Seattle Children's Hospital |
EPIC Observational Study |
| Hematology |
Ferguson |
Fletcher Allen |
Phase II Research Study of Nifurtimox |
| Dermatology |
Siegfried |
Pierre Fabre |
Infantile Hemangiomas Study |
| Endocrinology |
Tollefsen |
Eli Lilly |
The Genetics and Neuroendocrinology of Short Stature International Study |
| Hematology |
Puetz |
Biogen Idec Inc. |
An Open-Label, Multicenter Evaluation of Safety, BIIB031 |
| Hematology |
Ferguson |
Van Andel Institute |
NMRTC001 |
| Pulmonary |
Paruthi |
UCB Biosciences |
SP1004 Study Restless Leg Syndrome |
| Pulmonary |
Paruthi |
UCB Biosciences |
SP1005 Study Restless Leg Syndrome |
| Hematology |
Ferguson |
University of Vermont |
A Phase1 Trial of TPI 287 |
| Genetics |
Braddock |
University of California San Diego |
OTIS Autoimmune Diseases in Pregnancy Project |
| Pulmonary |
Wooldridge |
Cystic Fibrosis Foundation Therapeutics |
Fibrosing Colonopathy in US Patients with Cystic Fibrosis Treated with Pancreatic
Enzyme Replacement Therapy
|
| Gastro |
Teckman |
Genentech, Inc. |
A phase IIIb parallel group, open label study of pegylated interferon |
| Pulmonary |
Albers |
Hologic |
A Multi-Center Cystic Fibrosis Blood Sample Collection Study |
| Pulmonary |
Albers |
Kalobios Pharmaceuticals |
Study of KB001 A in Subjects with Cystic Fibrosis Infected with Pseudomonas aeruginosa |
| Hematology |
Ferguson |
Children's Hospital of Philadelphia |
COG industry Work Order |
| Pulmonary |
Albers |
Gilead Sciences |
Regimen of Inhaled Antibiotics for the Treatment of Chronic Pulmonary Pseudomonas
in Subjects with Cystic Fibrosis
|
| Pulmonary |
Wooldridge |
Vertex Pharmaceuticals |
Efficacy and Safety of Lumacaftor Monotherapy in Subjects Aged 12 Years and Older
with Cystic Fibrosis
|
| Hematology |
Ferguson |
Children's Hospital of Philadelphia |
A Phase I/II Trial of TPI 287 in Patients with Refractory or Recurrent Neuroblastoma
or Medulloblastoma NMTRC004
|
| Allergy |
Knutsen |
Baxter Healthcare Corp |
Safety, Tolerability, and Pharmacokinetics in Subjects with Primary Immunodeficiency
Diseases
|
| Hematology |
Puetz |
Biogen Idec Inc. |
Prevention and Treatment of Bleeding Episodes in Previously Treated Subjects With
Hemophilia A
|
| Hematology |
Ferguson |
Janssen Research Foundation |
Abciximab (ReoProR) as a Therapeutic Intervention for Sickle Cell Vaso-Occlusive Pain
Crisis
|
| Pulmonary |
Wooldridge |
Vertex Pharmaceuticals |
Ivacaftor in Subjects Aged 12 Years and Older With Cystic Fibrosis |
| Hematology |
Ferguson |
Spectrum Health Hospitals |
NMTRC 008 A Feasibility Trial using Molecular-Guided Therapy for the Treatment of
Patients
|
| Hematology |
Ferguson |
Eli Lilly |
Prasugrel and Placebo in Pediatric Patients with Sickle Cell Disease |
| Hematology |
Ferguson |
Van Andel Institute |
Neuroblastoma in Remission - Protocol Number NMTRC 003 |
| Pulmonary |
Albers |
Novartis Pharmaceuticals |
Tobramycin Inhalation Powder (TIP) administered once daily in patients with cystic
fibrosis
|
| Hematology |
Puetz |
American Thrombosis and Hemostasis Network |
My Life, Our Future: A Hemophilia Genotyping Initiative Data and Sample Registry Repository |
| Hematology |
Ferguson |
Children's Hospital of Philadelphia |
COG Industry Work Order: FP17305 SUB102 02 GLENNON SANOFI AALL1131 WO |
| Gastro |
Teckman |
Alnylam - Alpha 1 |
Natural History Study |
| Gastro |
Teckman |
Gilead Sciences |
Gilead US 334-1112 |
| Nephrology |
Wood |
Amgen |
Cincalcet HCI in Pediatrics |
| Hematology |
Ferguson |
Van Andel Institute |
NMTRC 009 Molecular Guided therapy for the treatment of refractory cancers |
| Hematology |
Puetz |
Biogen Idec Inc. |
Biogen 998HB303 |
| Endocrinology |
Siska |
Novo Nordisk |
Novo Nordisk - NN2211-3659 Ellipse |
| Allergy |
Knutsen |
Hoffman LaRoche |
Acoustics - WB28182 |
| Endocrinology |
Myers |
Zafgen |
Zafgen ZAF 311 Trial of ZGN 440 Beloranib |
| Gastro |
Teckman |
Gilead Sciences |
Gilead US 334-1116 Ledipasvir/Sofosbuvir tx for Hep C in Children |
| Hematology |
Puetz |
Biogen Idec Inc. |
PUP Hemophilia A |